Have you ever wanted to know more about the drug development process and how patients and patient organizations like FPWR can engage with and inform the process? The National Organization for Rare Diseases (NORD) has developed a free educational series to help teach patients and families about the steps involved in developing a new drug treatment, particularly for rare diseases.
The goal of this educational series is to provide families with the knowledge to empower them to effectively engage with and contribute to the drug development process. Modules will continue to be released throughout the year. The current modules provide an overview of the drug development process, including: discovery and development; preclinical research in cells and animal models; clinical research in humans; FDA review; and then post-market safety monitoring for drugs that are approved.
The course presents ways that patients and patient organizations can engage with each step of the process and make important contributions. The course also discusses some of the unique challenges specific to rare diseases along the way.
FPWR funds research, resources, and programs all along the drug development pathway, and these are highlighted in the graphic below. This excellent course from NORD, specifically designed for patients, is a great resource for families with rare diseases like PWS to learn more about each stage of the drug development process in more detail. If you are interested in taking the course, please click here.
If you are interested in taking the course, please click here.